top of page

BioSpace 's article on uniQure's path for Huntington's gene therapy clouded by ethical questions as potential phase 3 looms.

  • katrina4384
  • 11 hours ago
  • 1 min read
s
s

“To go back in a rare disease for sham surgeries is unethical,” Katie Jackson, president and CEO of Help 4 HD International, told BioSpace. “You’re asking people to get a sham surgery and sit in a placebo-like hold for one year, two years, three years,” preventing patients from participating in other clinical trials or from being able to receive AMT-130 in a future open-label extension study if they become too ill.


 
 
 

Comments


Subscribe Form

  • facebook
  • instagram
  • twitter

©2025 by Help 4 HD International.

bottom of page