BioSpace 's article on uniQure's path for Huntington's gene therapy clouded by ethical questions as potential phase 3 looms.
- katrina4384
- 11 hours ago
- 1 min read

“To go back in a rare disease for sham surgeries is unethical,” Katie Jackson, president and CEO of Help 4 HD International, told BioSpace. “You’re asking people to get a sham surgery and sit in a placebo-like hold for one year, two years, three years,” preventing patients from participating in other clinical trials or from being able to receive AMT-130 in a future open-label extension study if they become too ill.





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