As I sat down in the plush green chair across from my therapist, I knew we were going to spend much of the day’s session talking about the stresses of being a caregiver. I didn’t want to talk about endless hours I dedicate to my dad’s care, but my frustration that few people in my life understand the amount of effort it takes, both mentally and emotionally. This lack of understanding and acknowledgement has left me feeling extremely angry and alone. I know I am not the only o

LEXINGTON, Mass. and AMSTERDAM, Dec. 04, 2025 (GLOBE NEWSWIRE) -- uniQure N.V. (NASDAQ: QURE), a leading gene therapy company advancing transformative therapies for patients with severe medical needs, today announced that the company received final meeting minutes from the U.S. Food and Drug Administration (FDA) regarding a pre-Biologics License Application (BLA) meeting held on October 29, 2025 to discuss the application for AMT-130, an investigational gene therapy for Hunt

FDA Contacts: Emails OCOD@FDA.HHS.gov patientaffairs@fda.hhs.gov ombuds@oc.fda.gov Physical Address Food and Drug Administration Center for Biologics Evaluation and Research (CBER) 10903 New Hampshire Avenue Silver Spring, MD 20993-0002 Template One: Subject: Urgent: FDA Reconsider Accelerated Approval for uniQure’s AMT-130 Therapy in Huntington’s Disease   Dear FDA CBER - We face a critical moment in the fight against Huntington’s disease. The FDA’s recent hesitation in allo

Katie Jackson, CEO of Help 4 HD, was asked her initial response to the news today. We wanted to share that response with our community....